{"id":2233,"date":"2023-06-21T16:14:10","date_gmt":"2023-06-21T16:14:10","guid":{"rendered":"https:\/\/avaeh.org\/web_nueva_2021\/?p=2233"},"modified":"2023-06-27T16:18:44","modified_gmt":"2023-06-27T16:18:44","slug":"ptc-therapeutics-comparte-datos-provisionales-positivos-del-ensayo-clinico-pivot-hd-en-pacientes-con-enfermedad-de-huntington","status":"publish","type":"post","link":"https:\/\/avaeh.org\/web_nueva_2021\/2023\/06\/21\/ptc-therapeutics-comparte-datos-provisionales-positivos-del-ensayo-clinico-pivot-hd-en-pacientes-con-enfermedad-de-huntington\/","title":{"rendered":"PTC Therapeutics comparte datos provisionales positivos del ensayo cl\u00ednico PIVOT-HD en pacientes con enfermedad de Huntington"},"content":{"rendered":"\n<p class=\"wp-block-paragraph\">\u00ab<strong>Acerca de PTC518<br><\/strong>PTC est\u00e1 desarrollando un tratamiento potencial para la enfermedad de Huntington basado en nuestra tecnolog\u00eda de plataforma de empalme.\u00a0PTC518, una peque\u00f1a mol\u00e9cula que se puede tomar por v\u00eda oral, reduce la producci\u00f3n de la prote\u00edna Huntingtina mutada que provoca lesi\u00f3n y muerte de la neurona, lo que da como resultado la progresi\u00f3n de la enfermedad.\u00a0La peque\u00f1a mol\u00e9cula biodisponible por v\u00eda oral penetra la barrera hematoencef\u00e1lica, es selectiva, titulable y no se expulsa, que son propiedades de diferenciaci\u00f3n clave.\u00bb<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/ir.ptcbio.com\/news-releases\/news-release-details\/ptc-therapeutics-shares-positive-interim-data-pivot-hd-clinical\" target=\"_blank\" rel=\"noreferrer noopener\">LINK A LA WEB PTC THERAPEUTICS<\/a><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u00abAcerca de PTC518PTC est\u00e1 desarrollando un tratamiento potencial para la enfermedad de Huntington basado en nuestra tecnolog\u00eda de plataforma de empalme.\u00a0PTC518, una peque\u00f1a mol\u00e9cula que se puede tomar por v\u00eda oral, reduce la producci\u00f3n de la prote\u00edna Huntingtina mutada que provoca lesi\u00f3n y muerte de la neurona, lo que da [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-2233","post","type-post","status-publish","format-standard","hentry","category-sin-categoria"],"_links":{"self":[{"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/posts\/2233","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/comments?post=2233"}],"version-history":[{"count":1,"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/posts\/2233\/revisions"}],"predecessor-version":[{"id":2234,"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/posts\/2233\/revisions\/2234"}],"wp:attachment":[{"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/media?parent=2233"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/categories?post=2233"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/avaeh.org\/web_nueva_2021\/wp-json\/wp\/v2\/tags?post=2233"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}